| REVIEW ARTICLE |
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| Year : 2019 | Volume
: 5
| Issue : 2 | Page : 78-84 |
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Newer advances in the treatment of Duchenne muscular dystrophy and spinal muscular atrophy
Mukesh Kumar, Venugopalan Y Vishnu
Department of Neurology, All India Institute of Medical Sciences, New Delhi, India
Correspondence Address:
Venugopalan Y Vishnu
Department of Neurology, Room No. 704, CN Center, All India Institute of Medical Sciences, New Delhi - 110 029
India
 Source of Support: None, Conflict of Interest: None  | Check |
DOI: 10.4103/jcrsm.jcrsm_44_19
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Duchenne muscular dystrophy (DMD) and spinal muscular atrophy (SMA) are two common and important Inherited neuromuscular disorders which have witnessed immense advances in their treatment owing to ongoing developments in gene therapy. Better modalities for clinical testing and improved clinical awareness has led to facilitation of innovative therapeutic research. Multiple new agents have been approved by regulatory authorities. A continuing research on evaluating such treatment options is required more than ever. These novel therapies have immense potential to transform this field and prolong the functional independence and lifespan of patients.
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